Clinical Study
The HERO (Help Reduce organic Acids) Study
The HERO study is evaluating an experimental drug for methylmalonic acidemia (MMA) and propionic acidemia (PA). The study drug, called HST5040, is an oral therapy designed to correct metabolic abnormalities associated with MMA and PA. HERO will be conducted at select leading childrens hospitals in the United States. The HERO Study is recruiting participants age 2 and older with MMA or PA. The study is not enrolling patients who have had transplants at this time.
For more information contact:
Carrie Bailey
carrie.bailey@hsc.utah.edu
8015873605
IRB#: IRB_00142396
| PI: Nicola Longo
| Department: PEDIATRIC GENETICS
| Approval Date: 2021-09-15 06:00:00
Specialties: Pediatric Genetics
Who can participate?
Gender: All
Age: All Ages
Volunteers: Volunteers with special conditions
Location: In Person
Will I be paid for my time?
Yes